Liver issues, including a buildup of fat in the liver, occur before the onset of neuromuscular disease, per a study in a mouse model of SMA.

For columnist Alyssa Silva, advances in the development of SMA treatments have felt like glimmers of miracles.

Cure SMA is leading an advocacy campaign seeking new research funding to address unmet challenges for people with SMA.

Study using a new, child-friendly scale found patients up to age 2 had smaller mouth openings than healthy peers, risking ...